Lysosomal Disorders 1

August 11, 2023

The Lysosomal Disorders 1 session will be discussing MPSI-VII, Oligosaccharidoses, Mucolipidoses.

Commercial Supporter 

This educational activity is supported by an educational grant from Ultragenyx.

Learning Objectives

At the conclusion of this session, participants should be able to: 

  • Enumerate the manifestations of lysosomal storage diseases on different organ systems
  • Understand the different approaches to treating lysosomal storage diseases
  • Appreciate the known reasons for variability in mucopolysaccharidoses, Pompe, Gaucher and Fabry disease
Course summary
Available credit: 
  • 1.50 AMA PRA Category 1 Credit™
  • 1.50 Attendance
Course opens: 
Course expires: 
Event starts: 
08/11/2023 - 12:00pm MDT
Event ends: 
08/11/2023 - 1:30pm MDT
Children's Hospital Colorado - Virtual
Aurora, CO 80045
United States

Guest Faculty

William Wilcox, MD, PhD
Emory University


William Wilcox, MD, PhD, speaker for this activity, is on the advisory board for Sanofi-Genzyme, Chiesi and Takeda, is a principle investigator on contracted clinical research for Amicus Therapeutics, BioMarin, Protalix, Chiesi, Takeda, Alexion/AstraZeneca, 4D Molecular Therapeutics, Sangamo, Astellas, Denali, Cyclo Therapeutics and Pfizer, is a consultant for Spark Therapeutics/Roche and UniQure, and has received a research grant from Amicus Therapeutics and Takeda. 

Planners, faculty, and others in control of content (either individually or as a group) have no relevant financial relationships with ineligible companies.

All of the relevant financial relationships listed have been mitigated. 


Children’s Hospital Colorado is accredited by the Accreditation Council for Continuing Medical Education to provide continuing medical education for physicians.

Children’s Hospital Colorado designates this Live activity for a maximum of 1.50 AMA PRA Category 1 Credit(s)™. Physicians should only claim credit commensurate with the extent of their participation in the activity.


A general certificate of attendance will be available after the completion of the online evaluation. Claim only credit commensurate of your conference attendance.

Available Credit

  • 1.50 AMA PRA Category 1 Credit™
  • 1.50 Attendance


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